Gene-editing technologies show great promise for medical treatments and research, with the potential to cure thousands of ...

Same cuts, different responses Gene editing uses a protein called Cas9 as molecular scissors to cut targeted DNA and change its sequence. In the new study, the scientists discovered that gene editing ...

A new study in Nature Communications could influence how gene therapies are designed for many genetic diseases. Pictured: Gokul Ramadoss, the first author, is a PhD candidate in Bruce Conklin's lab at ...

Vertex Pharmaceuticals has two clinical-stage programs for type 1 diabetes, each employing different methods for preventing the immune system from rejecting the cell therapies. For a third program in ...

Megan Molteni reports on discoveries from the frontiers of genomic medicine, neuroscience, and reproductive tech. She joined STAT in 2021 after covering health and science at WIRED. You can reach ...

Despite the copious demands of his administrative positions as the White House chief science advisor (and until last year, the director of the NIH), Francis Collins, MD, PhD, has continued to run a ...

Many writers grouse when an editor makes a change in a story, but the consequences of changing a single word usually aren’t that dire. Not so with genetic instructions for making proteins. Even a ...