Sickle cell disease (SCD) is a genetic disorder that disproportionately affects African populations, with over 75% of global cases found in sub-Saharan Africa. 1 SCD continues to be the most common ...

Please provide your email address to receive an email when new articles are posted on . Two studies highlight the potential of gene editing for sickle cell disease treatment. Despite increasing ...

Essentially all cells in an organism's body have the same genetic blueprint, or genome, but the set of genes that are actively expressed at any given time in a cell determines what type of cell it ...

Forbes contributors publish independent expert analyses and insights. William A. Haseltine, Ph.D., covers genomics and regenerative medicine This voice experience is generated by AI. Learn more. This ...

For years, cell and gene therapies were mainly associated with rare and orphan diseases, those that impact small patient groups and lack effective treatment options. However, recent developments in ...

This story is the first in an occasional series following Louisiana’s first patients to receive gene therapy for sickle cell disease. On the third floor of Manning Family Children’s Hospital in New ...

Sickle cell disease is the scourge of a person’s red blood cells. The inherited blood disorder, which disproportionately affects people in sub-Saharan Africa and India, can cause unbearable pain ...

Will Shrank, MD, in December 2025 unveiled a new plan for managing the high costs of an expected future wave of gene-based treatments as many drugmakers seek to more broadly apply the kind of ...